Regulatory Strategies for Accelerating the Translation of Gene Therapies to Clinical Practice: Focus on GMO Considerations.Authors: Delgadillo J, Martin F, Carmona G, Canals JM, Rio P, Eguizabal C, Prosper F, Avendaño-Solá C08/2025 - Human gene therapy
CD44-targeted N-benzyltetrahydroisoquinoline derivatives as anticancer agents with high tumor-to-normal cell selectivity.Authors: Romero-Tamudo S, Carrión MD, Chayah M, Espejo-Román JM, Domene C, Sánchez-Martín RM, Cruz-López O, Conejo-García A08/2025 - European journal of medicinal chemistry
Off-target effects in CRISPR-Cas genome editing for human therapeutics: Progress and challenges.Authors: Kalter N, Fuster-García C, Silva A, Ronco-Díaz V, Roncelli S, Turchiano G, Gorodkin J, Cathomen T, Benabdellah K, Lee C, Hendel A07/2025 - Molecular therapy. Nucleic acids