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GenE-Humdi – Genome Editing for the treatment of human Disease Network

GenE-Humdi – Genome Editing for the treatment of human Disease Network

Program SPARK THERAPUTICS INC

Program SPARK THERAPUTICS INC

3TR

3TR

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CD44-targeted N-benzyltetrahydroisoquinoline derivatives as anticancer agents with high tumor-to-normal cell selectivity.

Authors: Romero-Tamudo S, Carrión MD, Chayah M, Espejo-Román JM, Domene C, Sánchez-Martín RM, Cruz-López O, Conejo-García A

08/2025 - European journal of medicinal chemistry

Off-target effects in CRISPR-Cas genome editing for human therapeutics: Progress and challenges.

Authors: Kalter N, Fuster-García C, Silva A, Ronco-Díaz V, Roncelli S, Turchiano G, Gorodkin J, Cathomen T, Benabdellah K, Lee C, Hendel A

07/2025 - Molecular therapy. Nucleic acids

Optimized network inference for immune diseased single cells.

Authors: Tejero EM, Vaz DJ, Barturen G, Rivas-Torrubia M, Alarcón-Riquelme ME, Kolch W, Matallanas D

07/2025 - Frontiers in immunology

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